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Sickle cell disease has a functional cure sitting on the shelf, and in the first full year of commercial use only 64 people worldwide completed treatment with the leading one. That figure covers infusions of Casgevy across both approved conditions in 2025, drawn from the manufacturer’s full year earnings. Roughly 100,000 Americans live with sickle […] The post Sickle cell gene therapy that few patients can reach appeared first on Rolling Out .